Niemann Pick type C - PIAM farmaceutici s.p.a

Niemann Pick type C is a disease of lysosomal lipid accumulation: patients with this disease are unable to metabolise lipids (e.g. cholesterol) properly, and they tend to accumulate lipids in the liver, spleen and other organs. The prevalence in the general population is about 1/100,000. The disease is characterized by autosomal recessive transmission and can […]

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

NIEMANN PICK C

Niemann-Pick disease type C

Niemann-Pick Type C Disease Biomarker and Clinical Endpoint Initiative - Ara Parseghian Medical Research Fund

Niemann-Pick Disease Concise Medical Knowledge

Niemann-Pick disease Information

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

Type 1 Tyrosinemia (HT-1) - PIAM farmaceutici s.p.a